Optimising Regulatory Strategies for Orphan Drugs

Optimising Regulatory Strategies for Orphan Drugs
Discover the strategies and insights needed to navigate orphan drug regulations effectively. This course provides essential guidance on regulatory processes that accelerate development and access, along with first-hand advice on how to maximise opportunities for rare disease medicines.







When:
10 November 2026
Where: Online 
Time: 09:30-15:30 GMT | 10:30-16:30 CET
CPD: 8 CPD hours upon successful completion

Who should attend

This course is ideal for:

  • Regulatory affairs professionals who are interested in biotechnology and innovative medicines
  • Those who are working for organisations that are targeting medicine innovation

What you'll learn

By completing this course, you will be able to:  

  • Acquire key information about regulatory processes that support early access to innovative medicines
  • Apply practical guidance for preparing and managing orphan drug submissions
  • Gain first-hand insights on how to optimise opportunities under orphan drug regulations
  • Navigate Orphan Medicinal Product legislation and its requirements
  • Gain insights into both EU and global approaches to orphan drug designation

Course overview 

This course offers a comprehensive understanding of the opportunities and challenges within orphan drug regulations, from both an EU and global perspective. It covers key topics such as orphan medicinal product legislation and the process of obtaining and maintaining orphan drug designation, providing practical guidance to support the development of medicines for rare diseases.

Course presenters 

Course presenters will be announced in the near future.

Pricing

 Standard training course registration fees
 Event Registration Type Price (GBP)
 Standard Price 
 TOPRA Member
£650.00 + VAT*
 Standard Price
 Non-member
£910.00 + VAT* 







 
Those working for regulatory or government agencies, academic institutions, charities, patient groups, emerging markets, and MSEs (Micro and Small Enterprises) can also access discounted rates by becoming a TOPRA member. For more information about the discounts available, please email meetings@topra.org before making your booking. 

Important Notice On VAT
In compliance with regulations, a *20% VAT will be charged to attendees only where applicable. If you have a VAT number or if the company or organisation you are affiliated with has a VAT number or equivalent please ensure it is visible on your profile. If your VAT number is not visible on your profile, please email finance@topra.org to have it updated. If you do not have a VAT number, there is no action required — VAT will be applied accordingly during the registration process. Please observe that the VAT number needs to be valid.

Click here to check and validate your VAT number.
For EU countries; if you are unsure of the VAT number, click here to check and validate your VAT number.

Terms and conditions

By booking a place on this course you are agreeing to the Training Terms and Conditions.

 
When
10/11/2026 09:00 - 17:00
Where
Online
Sign in or create an account to register Last day to register is 09/11/2026
My registration status: Not registered
Please complete your registration by adding any required items to your basket and proceeding to the checkout.
 
Your company name
Your VAT country
Your VAT number
NOTE
Important instructions before booking - If your company name or VAT number does not appear here or you would like to be invoiced using a different VAT number, please email finance@topra.org

Register now